2023 CSC 5k | Over $47,000 raised!

Thank you to over 370 runners, joggers, and walkers who joined us on Saturday, September 16, 2023, for our 6th annual Clinic for Special Children 5k. Over $47,000 was raised in support of the Clinic’s mission!

We couldn’t do this work without the support of many like the event sponsors, volunteers, participants, staff, and more! THANK YOU!

Stay tuned for details about our 2024 race.

International Study of TNNT1 Myopathy Establishes Operational Framework for Future Clinical Trials

STRASBURG, PA – A new study summarizes WiTNNess – a hybrid prospective/cross-sectional observational study of TNNT1 myopathy, a rare and lethal neuromuscular disease that causes progressive muscle weakness and stiffness, while cognitive and social development remain normal. The study aimed to identify clinically meaningful endpoints for future therapeutic trials following recent guidelines on natural history studies to support clinical trial readiness. The study was a broad collaborative effort led by clinicians and researchers at the Clinic for Special Children that included participants from around the globe and appears in the current issue of Annals of Clinical and Translational Neurology.

Read the full press release HERE

Read the paper HERE