In this edition of the CSC newsletter, read about the Watson family’s journey with GA-1, our partnership with the Strasburg Rail Road, new CSC staff members, recent research study updates, […]

THANK YOU to everyone who came out on Saturday, September 22nd and made our first Clinic for Special Children 5k such a success! Because of you and over 280 registrants, […]

STRASBURG, PA- A natural history study has provided the first comprehensive clinical description of spinal muscular atrophy (SMA) within the Amish and Mennonite communities and correlates ancestral chromosome 5 haplotypes […]

STRASBURG, PA- A new report has identified an alternative method to deliver nusinersen to patients with spinal muscular atrophy (SMA) using a subcutaneous intrathecal catheter system (SIC) configured by connecting […]

Please join us for our FIRST 5K Run/Jog/Walk to benefit Clinic for Special Children! $100 CASH PRIZE for overall top male & female runners! Enjoy a 5K, free refreshments, a […]

  In this edition of the CSC newsletter, read about the Martin family’s inspiring journey with Kleefstra Syndrome. Also in this issue is the story of Margaretha whom the Clinic […]

STRASBURG, PA- A new comprehensive natural history study about Amish nemaline myopathy (ANM) in the Old Order Amish population focuses on the promise of gene therapy for this lethal disorder. […]

Eugene and Jeanette Horning sat down with Lancaster Farming news to talk about their unique journey raising a special child living with a random gene deletion, only found in 15 […]

Dr. Katie Williams spent her last day at CSC on June 1st, traveling this week to continue her pediatric practice in her home state of Wisconsin. We would like to express […]

Please join us for our FIRST 5K Run/Jog/Walk to benefit Clinic for Special Children! Enjoy a 5K, free refreshments, a silent auction, and crafts for kids among the many family-friendly […]